Time- and dose-dependent normalization of pathological lysosomal storage and biochemistry in the mucopolysaccharidosis ΙΙΙΒ (MPS ΙΙΙΒ, Sanfilippo syndrome type Β) mouse model by intracerebroventricular enzyme replacement therapy with ΒΜΝ 250, a ΝAGLU-ΙGF2 fusion pro
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- 作者：Mika Aoyagi-Scharber ; Jon Vincelette ; Roger Lawrence ; Danielle Crippen-Harmon ; Bryan K. Yip ; Brian Baridon ; Heather Prill ; Wesley C. Minto ; Jeremy L. Van Vleet ; Catherine Vitelli ; Evan G. Adintori ; Terri Christianson ; Pascale M.N. Tiger ; Melanie J. Lo ; John Holtzinger ; Eric Chen ; Katherine A. Webster ; Jillian R. Brown ; Paul A. Fitzpatrick ; Jonathan H. LeBowitz ; Anil Bagri ; Sherry Bullens ; Brett E. Crawford ; Stuart Bunting
- 刊名：Molecular Genetics and Metabolism
- 出版年：2016
- 出版时间：February 2016
- 年：2016
- 卷：117
- 期：2
- 页码：S21
- 全文大小：50 K
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