Haploidentical Bone Marrow Transplantation with Post-Transplant Cyclophosphamide for Children and Adolescents with Fanconi Anemia

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• 作者：Carmem Bonfim¹ ; ^{carmembonfim@gmail.com} ; Lisandro Ribeiro¹ ; Samantha Nichele¹ ; Gisele Loth¹ ; Marco Bitencourt¹ ; Adriana Koliski¹ ; Cilmara Kuwahara¹ ; Ana Luiza Fabro¹ ; Noemi F. Pereira¹ ; Daniela Pilonetto¹ ; Monica Thakar² ; Hans-Peter Kiem³ ; Kristin Page⁴ ; Ephraim J. Fuchs⁵ ; Mary Eapen⁶ ; Ricardo Pasquini¹
• 关键词：Haploidentical ; Inherited bone marrow failure syndromes ; Fanconi anemia
• 刊名：Biology of Blood and Marrow Transplantation
• 出版年：2017
• 出版时间：February 2017
• 年：2017
• 卷：23
• 期：2
• 页码：310-317
• 全文大小：384 K
• 卷排序：23

文摘

Haploidentical transplantation using PT-CY expands access for FA patients without matched related or unrelated donors. High rates of hemorrhagic cystitis and viral reactivation were found. Haploidentical transplant using PT-CY results in acceptable overall survival comparable with other donor sources.