搜索页_+Morquio+A+Clinical+Assessment+Program

网站地图 | English | 公务邮箱

About the library

Background
History
Leadership
Organization

Opening Hours
Collections
Help Via Email

Electronic Information Resources

外文资源

内部出版物

SpringerLink电子期刊(2)

Elsevier电子期刊(2)

在“Elsevier电子期刊”中，命中：2条，耗时：0.1029499 秒

在所有数据库中总计命中：4条

1.Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome

作者：Christian J. Hendriksz^a ; ^{chris.hendriksz@srft.nhs.uk" class="auth_mail" title="E-mail the corresponding author} ; Rossella Parini^b ; Moeenaldeen D. AlSayed^c ; Julian Raiman^d ; Roberto Giugliani^e ; Martha L. Solano Villarreal^f ; John J. Mitchell^g ; Barbara K. Burton^h ; Norberto Guelbertⁱ ; Fiona Stewart^j ; Derralynn A. Hughes^k ; Kenneth I. Berger^l ; Peter Slasor^m ; Robert Matousek^m ; Elaina Jurecki^m ; Adam J. Shaywitz^m ; Paul R. Harmatzⁿ

关键词：3MSCT ; 3-minute stair climb test ; 6MWT ; 6-minute walk test ; AE ; adverse event ; ERT ; enzyme replacement therapy ; GALNS ; enzyme N-acetylgalactosamine-6-sulfatase ; IAR ; infusion-associated reaction ; IgE ; immunoglobulin E ; ITT ; intent-to-treat ; KS ; keratan sulfate ; MPP ; modified per-protocol ; MorCAP ; Morquio A Clinical Assessment Program ; NAb ; neutralizing antibody ; PBO ; placebo ; QOW ; every other week ; QW ; once weekly ; SAE ; serious adverse event ; TAb ; total antibody ; uKS ; urine keratan sulfate

刊名：Molecular Genetics and Metabolism

出版年：2016

2.The Morquio A Clinical Assessment Program: Baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects

作者：Paul Harmatz^a ; Karl Eugen Mengel^b ; Roberto Giugliani^c ; Vassili Valayannopoulos^d ; Shuan-Pei Lin^e ; Rossella Parini^f ; Nathalie Guffon^g ; Barbara K. Burton^h ; Christian J. Hendrikszⁱ ; John Mitchell^j ; Ana Martins^k ; Simon Jones^l ; Norberto Guelbert^m ; Ashok Vellodiⁿ ; Carla Hollak^o ; Peter Slasor^p ; Celeste Decker^p ; ^{cdecker@bmrn.com}

关键词：MPS ; Morquio ; GALNS ; Lysosomal storage disorder ; Endurance ; Respiratory function

刊名：Molecular Genetics and Metabolism

出版年：2013

1

按检索点细分(2)

题名(1)

关键词(1)

按出版年细分(2)

2016年(1)

2013年(1)

NGLC 2004-2010.National Geological Library of China All Rights Reserved.
Add:29 Xueyuan Rd,Haidian District,Beijing,PRC. Mail Add: 8324 mailbox 100083
For exchange or info please contact us via email.