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1.Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial
作者:Prof Jean Bennett ; MDup>aup>up> ; up>up>bup>up> ; up>up>dup>up> ; up>up>jebennet@mail.med.upenn.edu" class="auth_mail" title="E-mail the corresponding authorup> ; Jennifer Wellman ; MScup>dup>up> ; up>up>hup> ; Kathleen A Marshall ; COTup>dup> ; Sarah McCague ; BAup>dup> ; Manzar Ashtari ; PhDup>aup>up> ; up>up>bup>up> ; up>up>eup> ; Julie DiStefano-Pappas ; BAup>fup> ; Okan U Elci ; PhDup>fup> ; Daniel C Chung ; DOup>aup>up> ; up>up>bup>up> ; up>up>hup> ; Junwei Sun ; MScup>aup>up> ; up>up>dup> ; J Fraser Wright ; PhDup>dup>up> ; up>up>hup> ; Dominique R Cross ; MPHup>dup> ; Puya Aravand ; BAup>aup> ; Laura L Cyckowski ; BAup>eup> ; Jeannette L Bennicelli ; PhDup>aup>up> ; up>up>bup> ; Federico Mingozzi ; PhDup>dup>up> ; up>up>iup> ; Alberto Auricchio ; MDup>jup>up> ; up>up>kup> ; Eric A Pierce ; MDup>bup>up> ; up>up>cup>up> ; up>up>gup>up> ; up>up>lup> ; Jason Ruggiero ; MDup>cup> ; Prof Bart P Leroy ; MDup>dup>up> ; up>up>gup>up> ; up>up>mup> ; Prof Francesca Simonelli ; MDup>nup> ; Katherine A High ; MDup>dup>up> ; up>up>hup>up> ; up>up>oup> ; Prof Albert M Maguire ; MDup>aup>up> ; up>up>bup>up> ; up>up>cup>up> ; up>up>dup>up> ; up>up>gup>
刊名:The Lancet
出版年:2016
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